Keynote Presentation: Shaping the Future of Rare Diseases: A Blueprint for Patient-Driven Innovation

Session details:

This presentation shares our approach to supporting rare disease patients by fostering deep partnerships with advocacy groups and leveraging the extensive network of the Chiesi Group to reach as many patients as possible. We explore how collaboration and commitment help us push the boundaries of innovation and care. Central to our mission is understanding and measuring the societal burden on families living with rare diseases, ensuring that patient needs guide every step of research, development, and access efforts. Together, we strive to create lasting impact for patients and their communities.